Venugopal, V. & Pavlakis, S. Duchenne muscular dystrophy. StatPearls [Internet] https://www.ncbi.nlm.nih.gov/books/NBK482346/ (up to date 10 July 2023).
Guglieri, M. et al. JAMA Neurol. 79, 1005–1014 (2022).
Google Scholar
Syed, N. et al. Ann. Med. Surg. 87, 2529–2531 (2025).
Google Scholar
Aartsma-Rus, A. & Corey, D. R. Nucleic Acid Ther. 30, 67–70 (2020).
Google Scholar
Wilton-Clark, H. & Yokota, T. Medicine Immediately 57, 707–717 (2021).
Google Scholar
McDonald, C. M. et al. Lancet 390, 1489–1498 (2017).
Google Scholar
Hoy, S. M. Medicine 83, 1323–1329 (2023).
Google Scholar
Amoasii, L. et al. Science 362, 86–91 (2018).
Google Scholar
Tian, Y. et al. Nat. Biomed. Eng. https://doi.org/10.1038/s41551-026-01689-5 (2026).
Google Scholar
Shen, Y., Kim, I.-M. & Tang, Y. Cells 12, 892 (2023).
Google Scholar
